Psychiatry/Behavioral · PANCE / PANRE

Autism Spectrum Disorder (ASD)

Persistent deficits in social communication plus restricted/repetitive behaviors present in early development.

Also known as: autism, ASD, autism spectrum disorder

Overview

A neurodevelopmental disorder characterized by persistent deficits in social communication and social interaction across multiple contexts AND restricted, repetitive patterns of behavior, interests, or activities, with symptoms present in early developmental period and causing clinically significant impairment.

Epidemiology

Prevalence ~1 in 36 US children (CDC 2023). Male-to-female ratio ~4:1, though females may be underdiagnosed. Highly heritable (~80%).

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Question 1PsychiatryMedium
A 3-year-old boy is evaluated for delayed language and atypical social behavior. He makes little eye contact, does not point to share interest, and lines up his toy cars for long periods. He flaps his hands when excited and becomes distressed by changes in routine. He was born at term, and there is no history of neglect. Developmental evaluation confirms autism spectrum disorder. Which of the following best explains this child's disorder?
  • ALoss of MECP2 function producing regression and hand stereotypies after normal infancy
  • BAutoimmune destruction of striatal neurons following group A streptococcal infection
  • CEnvironmental lead neurotoxicity disrupting synaptic pruning in the developing cortex
  • DAtypical cortical development and connectivity from polygenic and copy-number variants
Reveal answer & full explanation
Correct answer: D — Atypical cortical development and connectivity from polygenic and copy-number variants
  • ALoss of MECP2 function producing regression and hand stereotypies after normal infancy
  • BAutoimmune destruction of striatal neurons following group A streptococcal infection
  • CEnvironmental lead neurotoxicity disrupting synaptic pruning in the developing cortex
  • DAtypical cortical development and connectivity from polygenic and copy-number variants

Why Atypical cortical development and connectivity from polygenic and copy-number variants is correct

  • Autism spectrum disorder is a highly heritable (~80%) neurodevelopmental disorder driven by polygenic inheritance plus copy-number variants and de novo mutations in synaptic and neurodevelopmental gene pathways.
  • These genetic contributions produce abnormal cortical development and atypical neural connectivity, particularly in regions subserving social cognition and language, explaining the social-communication deficits and restricted, repetitive behaviors present from the early developmental period.

Why the others are wrong

  • Loss of MECP2 function producing regression and hand stereotypies after normal infancy — this is Rett syndrome, which occurs almost exclusively in girls and requires loss of previously acquired language and purposeful hand use after a period of normal early development; this boy is male and has had persistent deficits without regression.
  • Autoimmune destruction of striatal neurons following group A streptococcal infection describes the PANDAS/Sydenham chorea mechanism (post-streptococcal basal ganglia autoimmunity producing abrupt-onset tics or OCD), not the early developmental, polygenic process of ASD.
  • Environmental lead neurotoxicity disrupting synaptic pruning in the developing cortex — lead exposure produces nonspecific cognitive, attentional, and behavioral impairment rather than the specific social-communication deficits and restricted, repetitive behaviors that define ASD, and no exposure is described.
Question 2PsychiatryMedium
A 2-year-old boy is brought in by his parents for delayed speech and limited social engagement. He uses no meaningful words, rarely makes eye contact, and does not point to show interest. He lines up his toy cars repeatedly and becomes very distressed when his routine changes, and he flaps his hands when excited. A failed M-CHAT-R/F prompted referral, and developmental evaluation confirms autism spectrum disorder. Audiology and lead screening are normal. He has no aggression, self-injury, or sleep disturbance. Which of the following is the most appropriate initial management?
  • ADefer intervention and reassess in six months
  • BObtain brain MRI and EEG before referral
  • CPrescribe sertraline for repetitive behaviors
  • DRefer for early intensive behavioral therapy
Reveal answer & full explanation
Correct answer: D — Refer for early intensive behavioral therapy
  • ADefer intervention and reassess in six months
  • BObtain brain MRI and EEG before referral
  • CPrescribe sertraline for repetitive behaviors
  • DRefer for early intensive behavioral therapy

Why Refer for early intensive behavioral therapy is correct

  • Early intensive behavioral intervention (ABA, naturalistic developmental behavioral interventions such as the Early Start Denver Model) plus speech-language and occupational therapy is the guideline-defined first-line management for a young child newly diagnosed with ASD.
  • Per AAP, intervention should begin as soon as ASD is suspected, and services should not be delayed pending formal diagnosis, because intervention before age 3 produces the largest developmental gains.
  • This child has core social-communication deficits and restricted/repetitive behaviors without irritability, anxiety, or sleep problems, so behavioral and developmental therapy is the appropriate initial step.

Why the others are wrong

  • Defer intervention and reassess in six months — the diagnosis is already established, and AAP guidance is to start services as soon as ASD is suspected; waiting six months at age 2 forfeits the developmental window in which intervention produces the largest gains.
  • Obtain brain MRI and EEG before referral — neuroimaging and EEG are not part of the routine ASD evaluation and are reserved for focal neurologic deficits, dysmorphic features, or suspected seizures, none of which are present here, so ordering them would only postpone therapy.
  • Prescribe sertraline for repetitive behaviors is incorrect because SSRIs are reserved for comorbid anxiety or OCD; evidence does not support them for core repetitive behaviors, and this child has no anxiety disorder.
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Risk factors

  • Male sex; sibling with ASD (recurrence risk ~10-20%)
  • Advanced parental age
  • Prematurity, low birth weight, perinatal complications
  • Genetic syndromes: fragile X, tuberous sclerosis, Rett (girls), 22q11.2 deletion
  • Valproate exposure in utero

Pathophysiology

Polygenic and copy-number variant contributions; abnormal cortical development and connectivity, particularly in regions subserving social cognition and language. Synaptic and neurodevelopmental gene pathways implicated.

Clinical presentation

Symptoms

  • Social communication: reduced social-emotional reciprocity, atypical nonverbal communication, difficulty developing and maintaining relationships appropriate to developmental level
  • Restricted/repetitive: stereotyped/repetitive motor movements or speech, insistence on sameness/routines, highly restricted fixated interests, hyper- or hyporeactivity to sensory input
  • Variable language ability — from non-speaking to fluent; pragmatic deficits common even in fluent speakers
  • Common co-occurrences: ID, ADHD, anxiety, epilepsy, GI symptoms, sleep disorders

Signs / physical exam

  • Reduced eye contact, limited joint attention, atypical play (lining up toys, lack of pretend play)
  • Echolalia, scripted speech
  • Hand-flapping, rocking, toe-walking
  • Sensory sensitivities (sound, texture, light)

Differential diagnosis

  • Intellectual disability without ASD — Cognitive impairment without disproportionate social communication deficits
  • Language disorder / social communication disorder — Language or pragmatic deficits without restricted/repetitive behaviors
  • ADHD — Inattention and impulsivity without core social-communication impairment; commonly co-occurs
  • Reactive attachment disorder — History of severe neglect; social withdrawal improves with stable caregiving
  • Selective mutism — Speaks at home but not in select settings; otherwise typical social development
  • Hearing impairment — Screen audiology in any child with language delay
  • Anxiety / OCD — Distinguish ego-dystonic compulsions from autistic restricted interests, which are typically ego-syntonic

Diagnostic workup

Diagnostic criteria

DSM-5-TR: (A) Persistent deficits in social communication and interaction across contexts — all three subcriteria (reciprocity, nonverbal communication, relationships); (B) Restricted/repetitive patterns — >=2 of four (stereotypies, insistence on sameness, restricted interests, sensory differences); (C) Symptoms in early developmental period; (D) Clinically significant impairment; (E) Not better explained by ID alone. Specify severity (levels 1-3 by support needs), with/without ID, language impairment, medical/genetic conditions, or catatonia. Screening: M-CHAT-R/F at 18 and 24 months.

Labs

  • Screen lead level, audiology evaluation
  • Genetic evaluation: chromosomal microarray and fragile X testing recommended for all; consider whole exome based on dysmorphology
  • Metabolic workup if regression or dysmorphic features
  • EEG if seizures suspected

Imaging

  • MRI not routine; obtain if focal findings, regression, microcephaly, or macrocephaly with neurologic signs

Diagnostic algorithm

ASD SeveritySocial communicationRestricted/repetitiveSupport need
Level 1Difficulty initiating; atypical responsesInflexibility hampers functionRequiring support
Level 2Marked deficits even with supportsDistress with change; obvious to observerSubstantial support
Level 3Severe deficits in functional communicationExtreme inflexibility, marked impairmentVery substantial support
DSM-5-TR Autism Spectrum Disorder severity levels.

Treatment

First-line

  • Early intensive behavioral intervention — applied behavior analysis (ABA), naturalistic developmental behavioral interventions (NDBI), Early Start Denver Model
  • Speech-language therapy; occupational therapy for sensory and motor issues
  • Educational supports — IEP, structured teaching
  • Family support and psychoeducation; respite care
  • Treat co-occurring conditions: ADHD, anxiety, sleep, epilepsy

Second-line / adjunct

  • Atypical antipsychotic — risperidone or aripiprazole (FDA-approved) for irritability/aggression/self-injury
  • SSRI for comorbid anxiety/OCD (avoid in repetitive behaviors alone — limited evidence)
  • Melatonin for sleep onset
  • Stimulants/non-stimulants for comorbid ADHD (response often less robust than in non-ASD ADHD)

Complications

  • Co-occurring intellectual disability (~30%), epilepsy (~20-30%), anxiety/OCD, ADHD, depression
  • Self-injurious behavior in severe cases
  • Sleep and feeding difficulties
  • Wandering/elopement
  • Higher rates of suicidality, especially in adults with ASD without ID
  • Caregiver burden

PANCE pearls

  • All children should be screened for ASD at 18 and 24 months using M-CHAT-R/F per AAP; refer for diagnostic evaluation if positive — do not wait.
  • Early intervention before age 3 produces the largest gains; do not delay services for formal diagnosis.
  • Catatonia is increasingly recognized in adolescents/adults with ASD — consider in regression with mutism, posturing.
  • Adults with ASD often present first with anxiety or depression; ask about lifelong social communication patterns.

References

  • AAP 2020 — Hyman SL et al. Identification, Evaluation, and Management of Children With Autism Spectrum Disorder. Pediatrics 2020
  • AACAP 2014 — AACAP Practice Parameter for the Assessment and Treatment of Children, Adolescents, and Adults with ASD (2014)
  • DSM-5-TR — American Psychiatric Association. DSM-5-TR (2022)

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